Rewriting RNA by editing exons – How it works

Ascidian Therapeutics represents a new generation of RNA therapeutics company.

Treating disease by replacing entire mutated exons at the RNA level has never before been possible. Today, Ascidian technology excises disease-causing exons and replaces them with wild-type exons to restore normal protein production – in a single reaction, with a single construct. See how:

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Ascidian Therapeutics RNA exon editing technology.